Gaucher disease is one member of a family of rare inherited diseases called lysosomal storage disorders (LSDs). In each one of these diseases, specific substances are stored in specialized compartments in the cells, known as lysosomes. Lysosomes digest and eliminate foreign substances or break down substances into energy for the body.
If you are a physician looking for more information about Shire HGT's treatment protocol for Gaucher disease, please contact OnePathSM by calling 1-866-888-0660 or contact us online. OnePathSM will direct inquiries to appropriate clinical trial management personnel.
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